CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect

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CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPR-Cpf1 mediates efficient homology-directed repair and temperature-controlled genome editing
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
NIR-II/CRISPR-Cas9 system optogenetic regulation of genome editing.
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Nanoparticles-mediated CRISPR-Cas9 gene therapy in inherited retinal diseases: applications, challenges, and emerging opportunities, Journal of Nanobiotechnology
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease phenotypes in a kidney organoid model - ScienceDirect
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPRi gene modulation and all-optical electrophysiology in post-differentiated human iPSC-cardiomyocytes
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease phenotypes in a kidney organoid model - Translational Research
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Genome-wide CRISPR/Cas9 deletion screen defines mitochondrial gene essentiality and identifies routes for tumour cell viability in hypoxia
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