Marta, with Niemann Pick C, fights for a cure with gene therapy
Por um escritor misterioso
Descrição
Marta is a four and a half year old girl with Niemann Pick C. This is a rare neurodegenerative genetic disease
Drug Delivery and Translational Research期刊最新论文, 化学/材料
High sphingomyelin levels induce lysosomal damage and autophagy
Gene Therapy for Niemann-Pick Type a Diseases Moves Forward
Rare performance to fight rare disease
News – Page 2 – Columbus Children's Foundation
Role the TICE? Arteriosclerosis, Thrombosis, and Vascular Biology
Gene therapy offers hope for Danish girl, but uncertainty lies ahead
Transmission Dynamics of a Mycobacterium tuberculosis Complex
Lysosomal cholesterol activates mTORC1 via an SLC38A9–Niemann-Pick
Clinical Case Reports: Vol 8, No 12
Hepatitis C Virus - Morphogenesis, Infection and Therapy
JBC Reviews: Journal of Biological Chemistry
The pathogenesis of Niemann–Pick type C disease: a role for
From Life-Changing Clinical Trials to Running for Rare: Justin's
A local family fights a rare disease and seemingly insurmountable odds
de
por adulto (o preço varia de acordo com o tamanho do grupo)
