Therapeutic intervention for Niemann–Pick type C disease must target
Por um escritor misterioso
Descrição
Consensus clinical management guidelines for Niemann-Pick disease type C, Orphanet Journal of Rare Diseases
Niemann-Pick Disease Type C (NP-C) Gene Therapy Activation Meeting (GAM) - International Niemann-Pick Disease Alliance (INPDA)
Niemann–Pick type C disease as proof‐of‐concept for intelligent biomarker panel selection in neurometabolic disorders - Papandreou - 2022 - Developmental Medicine & Child Neurology - Wiley Online Library
Niemann-Pick Disease, A Pipeline Analysis Report 2018, Technavio
Proposed pathological cascade in Niemann-Pick disease type C (NPC)
NPC1 enables cholesterol mobilization during long‐term potentiation that can be restored in Niemann–Pick disease type C by CYP46A1 activation
Understanding the phenotypic variability in Niemann-Pick disease type C (NPC): a need for precision medicine
Experimental treatment for Niemann-Pick disease type C1 appears safe, effective
PDF) Recent Advances in the Diagnosis and Treatment of Niemann-Pick Disease Type C in Children: A Guide to Early Diagnosis for the General Pediatrician
IJMS, Free Full-Text
IJMS, Free Full-Text
Combination therapy a potential strategy for treating Niemann-Pick disease
Potential treatment for Niemann-Pick type C, a rare neurodegenerative disease
de
por adulto (o preço varia de acordo com o tamanho do grupo)
